Laronidase

CAS 210589-09-6 1 FDA-DMF supplierBiologic

Overview

Laronidase is an enzyme replacement therapy used to treat patients with mucopolysaccharidosis I (MPS I), a lysosomal storage disorder caused by the deficiency of the enzyme alpha-L-iduronidase. It works by breaking down glycosaminoglycans that build up in cells over time, alleviating symptoms associated with the disorder.

Therapeutic areas

Genetic DisordersMetabolic Disorders

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