Avalglucosidase Alfa
CAS null 1 FDA-DMF supplierBiologic
Overview
Avalglucosidase alfa is a recombinant human enzyme used for treating Pompe disease, a genetic disorder characterized by the buildup of glycogen in the body's cells. It works by replacing the deficient enzyme acid alpha-glucosidase (GAA) in affected patients, helping to reduce glycogen accumulation.
Therapeutic areas
Genetic DisordersMetabolic Disorders
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