Sapropterin Dihydrochloride

Overview

Sapropterin Dihydrochloride is a synthetic form of tetrahydrobiopterin (BH4), a cofactor necessary for phenylalanine hydroxylase and the hydroxylases involved in the production of neurotransmitters such as dopamine and serotonin. It is used in the treatment of hyperphenylalaninemia in patients with phenylketonuria (PKU).

API suppliers (1)

Suppliers of Sapropterin Dihydrochloride backed by a verifiable FDA Type II Drug Master File. Source: FDA quarterly DMF list.

• DIPHARMA SA1 active DMF

Therapeutic areas