Genetic Disorders Companies
Browse 32 pharmaceutical and biotech companies active in Genetic Disorders — each profile screened against live FDA recalls, Warning Letters and Form 483 observations.
32 companies · FDA compliance signals on every profile
- Amicus Therapeutics, Inc.
- Amryt Pharma plc
- Andelyn Biosciences, Inc.
- BioMarin Pharmaceutical Inc.
- Biotech X Corporation
- Cellgen Diagnostics Inc.
- Cycle Pharmaceuticals Ltd.
- Editas Medicine, Inc.
- Fondazione Telethon
- GeneCure Biotech Inc.
- Genetic Therapies Inc.
- Novelna Inc.
- NS Pharma, Inc.
- Orphan Europe S.a.r.l.
- Prosensa Therapeutics B.V.
- Protalix BioTherapeutics, Inc.
- PTC Therapeutics, Inc.
- Rare Disease Research Global Inc.
- RareCare Pharmaceuticals Inc.
- RareGene Biotech Inc.
- Recordati Rare Diseases Inc.
- Regenxbio Inc.
- Retrophin, Inc.
- Sarepta Therapeutics, Inc.
- Shire Human Genetic Therapies, Inc.
- Silence Therapeutics Plc
- SkyBio Inc.
- Stichting Epigenetic Editing
- Ultragenyx Pharmaceutical Inc.
- Uniqure N.V.
- Voyager Therapeutics, Inc.
- Vybion, Inc.
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