Sebelipase Alfa
CAS 9025-79-2 1 FDA-DMF supplierBiologic
Overview
Sebelipase alfa is a recombinant form of the human lysosomal acid lipase enzyme used for enzyme replacement therapy in patients with lysosomal acid lipase deficiency. This rare genetic condition results in the accumulation of lipid droplets in various tissues due to the deficient activity of lysosomal acid lipase.
Therapeutic areas
Genetic DisordersLipid Metabolism Disorders
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