Exagamglogene Autotemcel
CAS 2872190-45-3 1 FDA-DMF supplierBiologic
Overview
Exagamglogene autotemcel is a gene therapy product designed to treat beta-thalassemia. It works by modifying a patient's own hematopoietic stem cells to produce functional beta-globin, thereby alleviating the symptoms of thalassemia major.
Therapeutic areas
HematologyGenetic Disorders
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