Cerliponase Alfa
CAS 1688275-21-8 1 FDA-DMF supplierBiologic
Overview
Cerliponase Alfa is a recombinant form of human tripeptidyl peptidase 1 (TPP1) used in enzyme replacement therapy for treating Batten disease, specifically CLN2 type. It acts by supplementing the deficient enzyme in patients, slowing disease progression.
Therapeutic areas
NeurologyGenetic Disorders
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